Browsing by Author "Kemper, Alex R"

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Discontinuation of thyroid hormone treatment among children in the United States with congenital hypothyroidism: findings from health insurance claims data

Kemper, Alex R; Ouyang, Lijing; Grosse, Scott D (BMC PEDIATRICS, 2010-02-15)
Immunodominant liver-specific expression suppresses transgene-directed immune responses in murine pompe disease.

Zhang, Ping; Sun, Baodong; Osada, Takuya; Rodriguiz, Ramona; Yang, Xiao Yi; Luo, Xiaoyan; Kemper, Alex R; ... (9 authors) (Hum Gene Ther, 2012-05)

Pompe disease can be treated effectively, if immune tolerance to enzyme replacement therapy (ERT) with acid α-glucosidase (GAA) is present. An adeno-associated viral (AAV) vector carrying a liver-specific regulatory cassette ...