Browsing by Author "Yen, PM"

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Adjunctive β2-agonist treatment reduces glycogen independently of receptor-mediated acid α-glucosidase uptake in the limb muscles of mice with Pompe disease.

Bird, A; Bursac, Nenad; Farah, BL; Koeberl, Dwight D; Li, S; Madden, L; Nance, S; ... (9 authors) (FASEB J, 2014-05)

Enzyme or gene replacement therapy with acid α-glucosidase (GAA) has achieved only partial efficacy in Pompe disease. We evaluated the effect of adjunctive clenbuterol treatment on cation-independent mannose-6-phosphate ...