Early HSCT corrects the skeleton in MPS.
Abstract
In this issue of Blood, Pievani et al have identified a potential solution to the
remaining barrier to the success of hematopoietic stem cell transplantation (HSCT)
in children with severe phenotype Hurler syndrome (mucopolysaccharidosis type I [MPS
I]).
Type
Journal articleSubject
AnimalsHumans
Bone Diseases, Developmental
Mucopolysaccharidosis I
Bone Marrow Transplantation
Female
Male
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https://hdl.handle.net/10161/24633Published Version (Please cite this version)
10.1182/blood-2014-11-606681Publication Info
Kurtzberg, Joanne (2015). Early HSCT corrects the skeleton in MPS. Blood, 125(10). pp. 1518-1519. 10.1182/blood-2014-11-606681. Retrieved from https://hdl.handle.net/10161/24633.This is constructed from limited available data and may be imprecise. To cite this
article, please review & use the official citation provided by the journal.
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Show full item recordScholars@Duke
Joanne Kurtzberg
Jerome S. Harris Distinguished Professor of Pediatrics
Dr. Kurtzberg is an internationally renowned expert in pediatric hematology/oncology,
pediatric blood and marrow transplantation, umbilical cord blood banking and transplantation,
and novel applications of cord blood and birthing tissues in the emerging fields of
cellular therapies and regenerative medicine. Dr. Kurtzberg serves as the Director
of the Marcus Center for Cellular Cures (MC3), Director of the Pediatric Transplant
and Cellular Therapy Program, Director of the Carolina

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