Early HSCT corrects the skeleton in MPS.

dc.contributor.author

Kurtzberg, Joanne

dc.date.accessioned

2022-03-23T19:06:14Z

dc.date.available

2022-03-23T19:06:14Z

dc.date.issued

2015-03

dc.date.updated

2022-03-23T19:06:13Z

dc.description.abstract

In this issue of Blood, Pievani et al have identified a potential solution to the remaining barrier to the success of hematopoietic stem cell transplantation (HSCT) in children with severe phenotype Hurler syndrome (mucopolysaccharidosis type I [MPS I]).

dc.identifier

S0006-4971(20)35184-3

dc.identifier.issn

0006-4971

dc.identifier.issn

1528-0020

dc.identifier.uri

https://hdl.handle.net/10161/24633

dc.language

eng

dc.publisher

American Society of Hematology

dc.relation.ispartof

Blood

dc.relation.isversionof

10.1182/blood-2014-11-606681

dc.subject

Animals

dc.subject

Humans

dc.subject

Bone Diseases, Developmental

dc.subject

Mucopolysaccharidosis I

dc.subject

Bone Marrow Transplantation

dc.subject

Female

dc.subject

Male

dc.title

Early HSCT corrects the skeleton in MPS.

dc.type

Journal article

duke.contributor.orcid

Kurtzberg, Joanne|0000-0002-3370-0703

pubs.begin-page

1518

pubs.end-page

1519

pubs.issue

10

pubs.organisational-group

Duke

pubs.organisational-group

School of Medicine

pubs.organisational-group

Clinical Science Departments

pubs.organisational-group

Institutes and Centers

pubs.organisational-group

Pathology

pubs.organisational-group

Pediatrics

pubs.organisational-group

Duke Cancer Institute

pubs.organisational-group

Institutes and Provost's Academic Units

pubs.organisational-group

Initiatives

pubs.organisational-group

Duke Innovation & Entrepreneurship

pubs.organisational-group

Pediatrics, Transplant and Cellular Therapy

pubs.publication-status

Published

pubs.volume

125

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