Gene therapy offers new hope for children with metachromatic leukodystrophy.

dc.contributor.author

Kurtzberg, Joanne

dc.date.accessioned

2022-03-23T14:27:10Z

dc.date.available

2022-03-23T14:27:10Z

dc.date.issued

2022-01

dc.date.updated

2022-03-23T14:27:10Z

dc.identifier

S0140-6736(22)00057-5

dc.identifier.issn

0140-6736

dc.identifier.issn

1474-547X

dc.identifier.uri

https://hdl.handle.net/10161/24562

dc.language

eng

dc.publisher

Elsevier BV

dc.relation.ispartof

Lancet (London, England)

dc.relation.isversionof

10.1016/s0140-6736(22)00057-5

dc.subject

Humans

dc.subject

Leukodystrophy, Metachromatic

dc.subject

Hematopoietic Stem Cell Transplantation

dc.subject

Child

dc.subject

Genetic Therapy

dc.title

Gene therapy offers new hope for children with metachromatic leukodystrophy.

dc.type

Journal article

duke.contributor.orcid

Kurtzberg, Joanne|0000-0002-3370-0703

pubs.begin-page

338

pubs.end-page

339

pubs.issue

10322

pubs.organisational-group

Duke

pubs.organisational-group

School of Medicine

pubs.organisational-group

Clinical Science Departments

pubs.organisational-group

Institutes and Centers

pubs.organisational-group

Pathology

pubs.organisational-group

Pediatrics

pubs.organisational-group

Duke Cancer Institute

pubs.organisational-group

Institutes and Provost's Academic Units

pubs.organisational-group

Initiatives

pubs.organisational-group

Duke Innovation & Entrepreneurship

pubs.organisational-group

Pediatrics, Transplant and Cellular Therapy

pubs.publication-status

Published

pubs.volume

399

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